Carnegie Mellon University

Breakthrough in RNA Research Could Lead to Treatment for Neuromuscular Disorders

Researchers from Carnegie Mellon University have discovered a way to target RNA that could lead to new treatment options for myotonic dystrophy type 1 (DM1), the most common adult-onset form of ...
Nature

Muscular dystrophies: causes and treatment

Muscular dystrophies are a group of more than 30 genetic disorders characterized by progressive muscle weakness and wasting. These disorders are typically associated with defects in muscle ...
Medscape

Therapy Insight: Cardiovascular Complications Associated With Muscular Dystrophy

The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...
WMUR

FDA expands approval of first gene therapy for rare form of muscular dystrophy

The U.S. Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the disease and a certain ...
WLWT

FDA expands approval of first gene therapy for rare form of muscular dystrophy

The Muscular Dystrophy Association trusts the decision of the FDA, which weighs the risks and benefits of the drug The Muscular Dystrophy Association trusts the decision of the FDA, which weighs the ...